Today "a milestone in the evolution of personalized therapies for rare & ultra-rare inborn errors of metabolism"
—the 1st human to undergo custom genome editing
—from decades of NIH funded research
https://www.nejm.org/doi/full/10.1056/NEJMe2505721
@nejm.org
https://www.nejm.org/doi/full/10.1056/NEJMoa2504747
https://www.nytimes.com/2025/05/15/health/gene-editing-personalized-rare-disorders.html?smid=nytcore-ios-share&referringSource=articleShare
—the 1st human to undergo custom genome editing
—from decades of NIH funded research
https://www.nejm.org/doi/full/10.1056/NEJMe2505721
@nejm.org
https://www.nejm.org/doi/full/10.1056/NEJMoa2504747
https://www.nytimes.com/2025/05/15/health/gene-editing-personalized-rare-disorders.html?smid=nytcore-ios-share&referringSource=articleShare
1 / 2
Comments