Exciting update from PTC Therapeutics ! The results from the 24mo PIVOT-HD study look great! Curious if the FDA considers accelerated approval with some kind of ph4 requirement for more post-approval data. Stoked to see *reductions* in NfL over 2 years in HD!

https://ir.ptcbio.com/static-files/c0babb34-ab5f-442b-8a92-8733a00efebf
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